Single-dose, subcutaneous recombinant phenylalanine ammonia lyase conjugated with polyethylene glycol in adult patients with phenylketonuria: An open-label, multicentre, phase 1 dose-escalation trial

Nicola Longo, Cary O. Harding, Barbara K. Burton, Dorothy K. Grange, Jerry Vockley, Melissa Wasserstein, Gregory M. Rice, Alejandro Dorenbaum, Jutta K. Neuenburg, Donald G. Musson, Zhonghua Gu, Saba Sile

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