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Dive into the research topics of 'Successful within-patient dose escalation of olipudase alfa in acid sphingomyelinase deficiency'. Together they form a unique fingerprint.- Sort by
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Melissa P. Wasserstein, Simon A. Jones, Handrean Soran, George A. Diaz, Natalie Lippa, Beth L. Thurberg, Kerry Culm-Merdek, Elias Shamiyeh, Haig Inguilizian, Gerald F. Cox, Ana Cristina Puga
Research output: Contribution to journal › Article › peer-review