Rescue of neurodegeneration in Niemann-Pick C mice by a prion-promoter-driven Npc1 cDNA transgene

Stacie K. Loftus, Robert P. Erickson, Steven U. Walkley, Mark A. Bryant, Arturo Incao, Randall A. Heidenreich, William J. Pavan

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71 Scopus citations

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Medicine & Life Sciences