Prospective study of the natural history of chronic acid sphingomyelinase deficiency in children and adults: eleven years of observation

Margaret M. McGovern, Melissa P. Wasserstein, Bruno Bembi, Roberto Giugliani, K. Eugen Mengel, Marie T. Vanier, Qi Zhang, M. Judith Peterschmitt

Research output: Contribution to journal › Article › peer-review

24 Scopus citations

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Medicine & Life Sciences