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Dive into the research topics of 'Olipudase alfa for treatment of acid sphingomyelinase deficiency (ASMD): safety and efficacy in adults treated for 30 months'. Together they form a unique fingerprint.- Sort by
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Melissa P. Wasserstein, George A. Diaz, Robin H. Lachmann, Marie Hélène Jouvin, Indrani Nandy, Allena J. Ji, Ana Cristina Puga
Research output: Contribution to journal › Article › peer-review