TY - JOUR
T1 - Enzyme replacement therapy in the home setting for mucopolysaccharidosis vi
T2 - A survey of patient characteristics and physicians' early findings in the united states
AU - Tifft, Cynthia
AU - Proud, Virginia
AU - Levy, Paul
AU - DeMarco, Kristin
AU - Nicely, Helen
AU - Turbeville, Sean
PY - 2009/1
Y1 - 2009/1
N2 - Galsulfase, a Food and Drug Administrationapproved enzyme replacement therapy for mucopolysaccharidosis VI, is administered once weekly in a hospital setting as a 4-hour intravenous infusion. To improve convenience and alleviate family responsibilities associated with clinic visits, some physicians are transitioning appropriate patients to home infusion therapy. An online survey was conducted with 3 physicians treating 4 patients with mucopolysaccharidosis VI to better understand the factors motivating the transition to home infusion therapy, identify characteristics of appropriate candidates, and evaluate the potential impact on the lives of patients and their families. Survey results showed that home infusion may offer patients and their families increased flexibility of schedule and enhanced family life.
AB - Galsulfase, a Food and Drug Administrationapproved enzyme replacement therapy for mucopolysaccharidosis VI, is administered once weekly in a hospital setting as a 4-hour intravenous infusion. To improve convenience and alleviate family responsibilities associated with clinic visits, some physicians are transitioning appropriate patients to home infusion therapy. An online survey was conducted with 3 physicians treating 4 patients with mucopolysaccharidosis VI to better understand the factors motivating the transition to home infusion therapy, identify characteristics of appropriate candidates, and evaluate the potential impact on the lives of patients and their families. Survey results showed that home infusion may offer patients and their families increased flexibility of schedule and enhanced family life.
UR - http://www.scopus.com/inward/record.url?scp=61749099059&partnerID=8YFLogxK
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U2 - 10.1097/NAN.0b013e31819228ee
DO - 10.1097/NAN.0b013e31819228ee
M3 - Article
C2 - 19142150
AN - SCOPUS:61749099059
SN - 1533-1458
VL - 32
SP - 45
EP - 52
JO - Journal of Infusion Nursing
JF - Journal of Infusion Nursing
IS - 1
ER -