Cyclodextrin alleviates neuronal storage of cholesterol in Niemann-Pick C disease without evidence of detectable blood-brain barrier permeability

Charles C. Pontikis, Cristin D. Davidson, Steven U. Walkley, Frances M. Platt, David J. Begley

Research output: Contribution to journalArticlepeer-review

71 Scopus citations

Fingerprint

Dive into the research topics of 'Cyclodextrin alleviates neuronal storage of cholesterol in Niemann-Pick C disease without evidence of detectable blood-brain barrier permeability'. Together they form a unique fingerprint.

Medicine & Life Sciences