A mouse model for mucopolysaccharidosis type III A (Sanfilippo syndrome)

Mantu Bhaumik, Vivienne J. Muller, Tina Rozaklis, Linda Johnson, Kostantin Dobrenis, Riddhi Bhattacharyya, Sarah Wurzelmann, Peter Finamore, John J. Hopwood, Steven U. Walkley, Pamela Stanley

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